Neuronal ceroid lipofuscinosis 11 (CLN11) presenting with early-onset cone-rod dystrophy and learning difficulties
Source: Neurogenetics
Evidence of the impact of CLN2 and CLN3 Batten disease on families in the United Kingdom
Source: Orphanet Journal of Rare Diseases
Novel surgical approach for intraventricular cerliponase alfa enzyme replacement therapy via central venous access device (CVAD) port in neuronal ceroid lipofuscinosis type 2 (CLN2) disease
Source: Child's Nervous System
Progranulin deficiency in the brain: the interplay between neuronal and non-neuronal cells
Source: Translational Neurodegeneration
TPCs: FROM PLANT TO HUMAN
Source: Physiological reviews
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