Clinical Benefit and Revenues of Drugs Affected by Rare Pediatric Disease Priority Review Vouchers, 2017-2023
Source: Journal of Pediatrics
Burden of rare genetic disorders in India: twenty-two years’ experience of a tertiary centre
Source: Orphanet Journal of Rare Diseases
Differential detection of megakaryocytic and erythroid DNA in plasma in hematological disorders
Source: npj Genomic Medicine
Global and regional cardiac magnetic resonance feature tracking left ventricular strain analysis in assessing early myocardial disease in β thalassemia major patients
Source: Journal of Cardiovascular Imaging
Homozygous hemoglobin Lepore disease in a child: A case report
Source: Pediatric Hematology Oncology Journal
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