A Drosophila model of mucopolysaccharidosis IIIB
Source: Genetics
Transplantation of Wild-Type Hematopoietic Stem and Progenitor Cells Improves Disease Phenotypes in a Mucopolysaccharidosis IIIC Mouse Model
Source: Cell Transplantation
Pediatric Interventions in a Sanfilippo Syndrome Patient Under General Anesthesia: A Case Report
Source: Case Reports in Dentistry
Behavioural disorders and sleep problems in Sanfilippo syndrome: overlaps with some other conditions and importance indications
Source: European Child and Adolescent Psychiatry
Extracellular vesicles from microglial cells activated by abnormal heparan sulfate oligosaccharides from Sanfilippo patients impair neuronal dendritic arborization
Source: Molecular Medicine
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