Substrate reduction using a glucosamine analogue in Drosophila melanogaster and mouse models of Sanfilippo syndrome
Source: Molecular Genetics and Metabolism
A Drosophila model of mucopolysaccharidosis IIIB
Source: Genetics
Rare Presentation of Attenuated Mucopolysaccharidosis Type IIIA as Isolated Retinitis Pigmentosa
Source: Journal of VitreoRetinal Diseases
Transplantation of Wild-Type Hematopoietic Stem and Progenitor Cells Improves Disease Phenotypes in a Mucopolysaccharidosis IIIC Mouse Model
Source: Cell Transplantation
Pediatric Interventions in a Sanfilippo Syndrome Patient Under General Anesthesia: A Case Report
Source: Case Reports in Dentistry
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